First test of a “high-density injection” protocol for myogenic cell transplantation throughout large volumes of muscles in a Duchenne muscular dystrophy patient: eighteen months follow-up

Conversion of mdx myofibres from dystrophin-negative to -positive by injection of normal myoblasts

T. Partridge, Jennifer E. Morgan, Gary R. Coulton et al. · Nature · 1989 · 862 citations

Medicine, Biophysics, Pathology +10

Cell Therapy of α-Sarcoglycan Null Dystrophic Mice Through Intra-Arterial Delivery of Mesoangioblasts

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Medicine, Bioengineering, Biotechnology +17

Systemic delivery of genes to striated muscles using adeno-associated viral vectors

Paul Gregorevic, Michael J. Blankinship, James M. Allen et al. · Nature Medicine · 2004 · 611 citations · Full text

Pharmacy, Bioengineering, Molecular Biology +14

Rescue of Dystrophic Muscle Through U7 snRNA-Mediated Exon Skipping

Aurélie Goyenvalle, Adeline Vulin, Françoise Fougerousse et al. · Science · 2004 · 477 citations

Life Sciences, Genetics, Molecular Biology +16

Practice Parameter: Corticosteroid treatment of Duchenne dystrophy [RETIRED]

Richard T. Moxley, Stephen Ashwal, S. Pandya et al. · Neurology · 2005 · 302 citations · Full text

Medicine, Neurology, Pediatrics +12