Xavier León

FGF21 gene therapy as treatment for obesity and insulin resistance

Verónica Jiménez, Claudia Jambrina, Estefanía Casana et al. · EMBO Molecular Medicine · 2018 · 329 citations · Full text

Life Sciences, Biochemistry, Biotechnology +17

High AAV vector purity results in serotype- and tissue-independent enhancement of transduction efficiency

Eduard Ayuso, Federico Mingozzi, Joel Montané et al. · Gene Therapy · 2009 · 278 citations

Life Sciences, Biotechnology, Molecular Biology +13

Characterization of a Recombinant Adeno-Associated Virus Type 2 Reference Standard Material

Martin Lock, Susan P. McGorray, Alberto Auricchio et al. · Human Gene Therapy · 2010 · 131 citations · Full text

Life Sciences, Biotechnology, Molecular Biology +14

Manufacturing and Characterization of a Recombinant Adeno-Associated Virus Type 8 Reference Standard Material

Eduard Ayuso, Véronique Blouin, Martin Lock et al. · Human Gene Therapy · 2014 · 89 citations · Full text

Life Sciences, Biotechnology, Molecular Biology +16

CNS-directed gene therapy for the treatment of neurologic and somatic mucopolysaccharidosis type II (Hunter syndrome)

Sandra Motas, Virginia Haurigot, Sara Marcó et al. · JCI Insight · 2016 · 61 citations · Full text

Pharmacy, Neurology, Neuroscience +17