Patricia A. O’Donnell

Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs

Katherine P. Ponder, John R. Melniczek, Lingfei Xu et al. · Proceedings of the National Academy of Sciences · 2002 · 169 citations · Full text

AAVrh10 Gene Therapy Ameliorates Central and Peripheral Nervous System Disease in Canine Globoid Cell Leukodystrophy (Krabbe Disease)

Allison M. Bradbury, Mohammed Rafi, Jessica Bagel et al. · Human Gene Therapy · 2018 · 90 citations · Full text

Immunology, Pathology, Central Nervous Systems +18

Transfusion of 28‐day‐old leucoreduced or non‐leucoreduced stored red blood cells induces an inflammatory response in healthy dogs

Mary Beth Callan, Reema Patel, Ann H. Rux et al. · Vox Sanguinis · 2013 · 76 citations · Full text

Transduction of Hepatocytes after Neonatal Delivery of a Moloney Murine Leukemia Virus Based Retroviral Vector Results in Long-Term Expression of β-Glucuronidase in Mucopolysaccharidosis VII Dogs

Lingfei Xu, Mark E. Haskins, John R. Melniczek et al. · Molecular Therapy · 2002 · 59 citations · Full text

Expression in blood cells may contribute to biochemical and pathological improvements after neonatal intravenous gene therapy for mucopolysaccharidosis VII in dogs

Bin Wang, Thomas O’Malley, Lingfei Xu et al. · Molecular Genetics and Metabolism · 2005 · 41 citations

Mucopolysaccharidosis Vii, Blood Cells, Veterinary Pathology +6