Mohammed Rafi

AAVrh10 Gene Therapy Ameliorates Central and Peripheral Nervous System Disease in Canine Globoid Cell Leukodystrophy (Krabbe Disease)

Allison M. Bradbury, Mohammed Rafi, Jessica Bagel et al. · Human Gene Therapy · 2018 · 90 citations · Full text

Immunology, Pathology, Central Nervous Systems +18

Insertion in the mRNA of a metachromatic leukodystrophy patient with sphingolipid activator protein-1 deficiency.

X L Zhang, Mohammed Rafi, Gregory D. DeGala et al. · Proceedings of the National Academy of Sciences · 1990 · 66 citations · Full text

Sap-1 Deficiency, Genetics, Immunology +21

Genetic galactocerebrosidase deficiency (globoid cell leukodystrophy, Krabbe disease) in rhesus monkeys (Macaca mulatta).

Gary B. Baskin, Marion S. Ratterree, Billie B. Davison et al. · PubMed · 1998 · 57 citations

Neurological Disorder, Genetics, Pathology +20

Cell-type-specific gene delivery into neuronal cells in vitro and in vivo

Zahida Parveen, Muḥammad Mukhtār, Mohammed Rafi et al. · Virology · 2003 · 19 citations

Cell-type-specific Gene Delivery, Cell-based Drug Delivery, In Vivo Gene Therapy +10