Thomas O’Malley

Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs

Katherine P. Ponder, John R. Melniczek, Lingfei Xu et al. · Proceedings of the National Academy of Sciences · 2002 · 169 citations · Full text

Enzyme Replacement Therapy in Feline Mucopolysaccharidosis I

Emil Kakkis, Edward H. Schuchman, Xingxuan He et al. · Molecular Genetics and Metabolism · 2001 · 89 citations

Enzyme Replacement Therapy, Pathogenesis, Veterinary Science +3

Long-term Amelioration of Feline Mucopolysaccharidosis VI After AAV-mediated Liver Gene Transfer

Gabriella Cotugno, Patrizia Annunziata, Alessandra Tessitore et al. · Molecular Therapy · 2010 · 72 citations · Full text

Biochemical, Pathological, and Skeletal Improvement of Mucopolysaccharidosis VI After Gene Transfer to Liver but Not to Muscle

Alessandra Tessitore, Armida Faella, Thomas O’Malley et al. · Molecular Therapy · 2007 · 70 citations · Full text

Transduction of Hepatocytes after Neonatal Delivery of a Moloney Murine Leukemia Virus Based Retroviral Vector Results in Long-Term Expression of β-Glucuronidase in Mucopolysaccharidosis VII Dogs

Lingfei Xu, Mark E. Haskins, John R. Melniczek et al. · Molecular Therapy · 2002 · 59 citations · Full text