Sukumar Nagendran

Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy

Jerry R. Mendell, Samiah Al-Zaidy, Richard Shell et al. · New England Journal of Medicine · 2017 · 2.3K citations · Full text

Medicine, Genetics, Neurology +16

AVXS-101 (Onasemnogene Abeparvovec) for SMA1: Comparative Study with a Prospective Natural History Cohort

Samiah Al-Zaidy, Stephen J. Kolb, Linda Lowes et al. · Journal of Neuromuscular Diseases · 2019 · 182 citations · Full text

Medicine, Neurology, Pediatrics +13

Impact of Age and Motor Function in a Phase 1/2A Study of Infants With SMA Type 1 Receiving Single-Dose Gene Replacement Therapy

Linda Lowes, Lindsay N. Alfano, W. David Arnold et al. · Pediatric Neurology · 2019 · 181 citations · Full text

Medicine, Neurology, Pediatrics +15

Impact of Metformin-Induced Gastrointestinal Symptoms on Quality of Life and Adherence in Patients with Type 2 Diabetes

Hermes Flórez, Jiacong Luo, Sumaya Castillo-Florez et al. · Postgraduate Medicine · 2010 · 110 citations

Pharmacy, Internal Medicine, Pharmacotherapy +17

The Effect of Colesevelam Hydrochloride on Insulin Sensitivity and Secretion in Patients With Type 2 Diabetes: A Pilot Study

Sherwyn Schwartz, Yu‐Ling Lai, Jianbo Xu et al. · Metabolic Syndrome and Related Disorders · 2010 · 44 citations · Full text

Medicine, Pharmacology, Pharmacotherapy +16