Statistics
Publications
329
Citations
49.7K
Authors
19
Location
Bannockburn, United States
329
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
Jerry R. Mendell, Samiah Al-Zaidy, Richard Shell et al. · New England Journal of Medicine · 2017 · 2.2K citations · Full text
Guy A. Van Hazel, Volker Heinemann, Navesh Sharma et al. · Journal of Clinical Oncology · 2016 · 339 citations
Ralf Ulrich Trappe, Daan Dierickx, Heiner Zimmermann et al. · Journal of Clinical Oncology · 2017 · 219 citations · Full text
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