W. David Arnold

Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy

Jerry R. Mendell, Samiah Al-Zaidy, Richard Shell et al. · New England Journal of Medicine · 2017 · 2.2K citations · Full text

The Chemical Nature of Hydrogen Bonding in Proteins via NMR: <i>J</i>-Couplings, Chemical Shifts, and AIM Theory

W. David Arnold, Eric Oldfield · Journal of the American Chemical Society · 2000 · 433 citations

Bond 3Hjnc, Molecular Biology, Protein Folding +20

Natural history of infantile‐onset spinal muscular atrophy

Stephen J. Kolb, Christopher S. Coffey, Jon Yankey et al. · Annals of Neurology · 2017 · 392 citations · Full text

Health outcomes in spinal muscular atrophy type 1 following AVXS‐101 gene replacement therapy

S. Al-Zaidy, A. Simon Pickard, Kavitha Kotha et al. · Pediatric Pulmonology · 2018 · 213 citations · Full text

Impact of Age and Motor Function in a Phase 1/2A Study of Infants With SMA Type 1 Receiving Single-Dose Gene Replacement Therapy

Linda Lowes, Lindsay N. Alfano, W. David Arnold et al. · Pediatric Neurology · 2019 · 176 citations · Full text