Scott McPhee

Dystrophin Immunity in Duchenne's Muscular Dystrophy

Jerry R. Mendell, Katherine Campbell, Louise R. Rodino‐Klapac et al. · New England Journal of Medicine · 2010 · 650 citations · Full text

Autoimmune Disease, Skeletal Muscle, Transgene Expression +11

Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

Dawn E. Bowles, Scott McPhee, Chengwen Li et al. · Molecular Therapy · 2011 · 390 citations · Full text

Engineering, In Vivo Gene Therapy, Immunology +19

Long-Term Follow-Up After Gene Therapy for Canavan Disease

Paola Leone, David Shera, Scott McPhee et al. · Science Translational Medicine · 2012 · 322 citations · Full text

Reengineering a receptor footprint of adeno-associated virus enables selective and systemic gene transfer to muscle

Aravind Asokan, Julia C Conway, Jana L. Phillips et al. · Nature Biotechnology · 2009 · 253 citations · Full text

Viral Replication, Signal Transduction, Gene Expression +11

Gene Therapy of Canavan Disease: AAV-2 Vector for Neurosurgical Delivery of Aspartoacylase Gene ( <i>ASPA</i> ) to the Human Brain

Christopher G. Janson, Scott McPhee, Larissa T. Bilaniuk et al. · Human Gene Therapy · 2002 · 251 citations