Louise R. Rodino‐Klapac

Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy

Jerry R. Mendell, Samiah Al-Zaidy, Richard Shell et al. · New England Journal of Medicine · 2017 · 2.2K citations · Full text

Eteplirsen for the treatment of Duchenne muscular dystrophy

Jerry R. Mendell, Louise R. Rodino‐Klapac, Zarife Sahenk et al. · Annals of Neurology · 2013 · 770 citations · Full text

Dystrophin Immunity in Duchenne's Muscular Dystrophy

Jerry R. Mendell, Katherine Campbell, Louise R. Rodino‐Klapac et al. · New England Journal of Medicine · 2010 · 650 citations · Full text

Autoimmune Disease, Skeletal Muscle, Transgene Expression +11

Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy

Jerry R. Mendell, Zarife Sahenk, Kelly J. Lehman et al. · JAMA Neurology · 2020 · 360 citations · Full text

Gentamicin‐induced readthrough of stop codons in duchenne muscular dystrophy

Vinod Malik, Louise R. Rodino‐Klapac, Laurence Viollet et al. · Annals of Neurology · 2010 · 271 citations · Full text