Long-Term Effect of Gene Therapy on Leber’s Congenital Amaurosis

James Bainbridge, Manjit Mehat, Venki Sundaram, +28

New England Journal of Medicine

Effective gene therapy with nonintegrating lentiviral vectors

Rafael J. Yáñez‐Muñoz, Kamaljit S. Balaggan, Angus MacNeil, +14

Nature Medicine

Gene TherapiesAntiviral TherapyGenetic EngineeringVirologyGene Vector +4

The Drusenlike Phenotype in Aging<i>Ccl2</i>-Knockout Mice Is Caused by an Accelerated Accumulation of Swollen Autofluorescent Subretinal Macrophages

Ulrich F. O. Luhmann, Scott Robbie, Peter Munro, +7

Investigative Ophthalmology & Visual Science

Assessment of ocular transduction using single-stranded and self-complementary recombinant adeno-associated virus serotype 2/8

M Natkunarajah, P. Trittibach, Jenny McIntosh, +5

Gene Therapy

Ocular DiseaseOphthalmologyOcular TransductionPathogenesisImmunology +4

Long-Term Survival of Photoreceptors Transplanted into the Adult Murine Neural Retina Requires Immune Modulation

Emma L. West, R. A. Pearson, Susie E. Barker, +7

Stem Cells

Gene therapy in the second eye of RPE65-deficient dogs improves retinal function

Matthew J. Annear, Joshua T. Bartoe, Susie E. Barker, +5

Gene Therapy

Gene TherapiesOcular DiseaseRetinaOphthalmologyExperimental Ophthalmology +7

Subretinal delivery of adeno‐associated virus serotype 2 results in minimal immune responses that allow repeat vector administration in immunocompetent mice

Susie E. Barker, Cathryn Broderick, Scott Robbie, +8

The Journal of Gene Medicine

EIAV vector-mediated delivery of endostatin or angiostatin inhibits angiogenesis and vascular hyperpermeability in experimental CNV

Kamaljit S. Balaggan, K. Binley, Margaret Esapa, +10

Gene Therapy

Translational MedicineAngiogenesisMedicineImmunologyEndothelial Dysfunction +8

Lentiviral-vector-mediated expression of murine IL-1 receptor antagonist or IL-10 reduces the severity of endotoxin-induced uveitis

P. Trittibach, Susie E. Barker, Cathryn Broderick, +8

Gene Therapy

InflammationEndotoxin-induced UveitisCytokineAllergyAutoimmune Disease +11

Targeted Gene Delivery to Human Airway Epithelial Cells with Synthetic Vectors Incorporating Novel Targeting Peptides Selected by Phage Display

Michele Writer, Barry J. Marshall, Michael A. Pilkington‐Miksa, +8

Journal of drug targeting