Robert T. Leshner

A Randomized Study of Alglucosidase Alfa in Late-Onset Pompe's Disease

Ans T. van der Ploeg, Paula R. Clemens, Deyanira Corzo et al. · New England Journal of Medicine · 2010 · 747 citations · Full text

Life Sciences, Internal Medicine, Pharmacotherapy +13

Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study

Craig M. McDonald, Erik Henricson, Richard T. Abresch et al. · The Lancet · 2017 · 475 citations

Medicine, Endocrinology, Neuromuscular Disorders +7

Clinical evaluator reliability for quantitative and manual muscle testing measures of strength in children

Diana M. Escolar, Erik Henricson, J. Mayhew et al. · Muscle & Nerve · 2001 · 250 citations

Education, Physical Medicine, Exercise Testing +14

Prednisone/prednisolone and deflazacort regimens in the CINRG Duchenne Natural History Study

Luca Bello, Heather Gordish‐Dressman, Lauren P. Morgenroth et al. · Neurology · 2015 · 222 citations · Full text

Pharmacy, Pharmacotherapy, Rehabilitation Medicine +15

Dietary erucic acid therapy for X‐linked adrenoleukodystrophy

William B. Rizzo, Robert T. Leshner, A. Odone et al. · Neurology · 1989 · 205 citations

Life Sciences, Biochemistry, Nutritional Sciences +17