Concepedia
2
Publications
79
Citations
H-Index
2021
Active since
Affiliations
Boston Children's Hospital(Current)
Dorothea Holzwarth is an author at Boston Children's Hospital.
Publications per year
2021–2025
Safety Monitoring of Gene Therapy for Spinal Muscular Atrophy with Onasemnogene Abeparvovec –A Single Centre Experience
Johannes Friese, Stephanie Geitmann, Dorothea Holzwarth et al. · Journal of Neuromuscular Diseases · 2021 · 66 citations · Full text
Safety and efficacy of apitegromab in nonambulatory type 2 or type 3 spinal muscular atrophy (SAPPHIRE): a phase 3, double-blind, randomised, placebo-controlled trial
Thomas O. Crawford, Eugenio Mercuri, Heike Kölbel et al. · The Lancet Neurology · 2025 · 13 citations · Full text
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