Safety and efficacy of apitegromab in nonambulatory type 2 or type 3 spinal muscular atrophy (SAPPHIRE): a phase 3, double-blind, randomised, placebo-controlled trial - Concepedia

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Safety and efficacy of apitegromab in nonambulatory type 2 or type 3 spinal muscular atrophy (SAPPHIRE): a phase 3, double-blind, randomised, placebo-controlled trial

DOI Full Paper Access

13

Citations

18

References

2025

Year

Thomas O. Crawford, Eugenio Mercuri, Heike Kölbel, Nancy L. Kuntz, Richard S. Finkel, Jena M. Krueger, Kaitlin Batley, Sally Dunaway Young, Jing L. Marantz, Guochen Song,

The Lancet Neurology

References

	Year	Citations

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