Nusinersen in type 1 spinal muscular atrophy: Twelve‐month real‐world data

Marika Pane, Giorgia Coratti, Valeria Sansone, +20

Annals of Neurology

Nusinersen in type 1 SMA infants, children and young adults: Preliminary results on motor function

Marika Pane, Concetta Palermo, Sonia Messina, +15

Neuromuscular Disorders

Type 1KinesiologyMotor DevelopmentPediatricsSma Infants +4

Respiratory Needs in Patients with Type 1 Spinal Muscular Atrophy Treated with Nusinersen

Valeria Sansone, Alice Pirola, Emilio Albamonte, +21

The Journal of Pediatrics

Type 1Spinal Cord InjuryPulmonary CareRespiratory NeedsPulmonary Medicine +3

Upper limb function in Duchenne muscular dystrophy: 24 month longitudinal data

Marika Pane, Giorgia Coratti, Claudia Brogna, +36

PLoS ONE

Clinical Variability in Spinal Muscular Atrophy Type <scp>III</scp>

Giorgia Coratti, Sonia Messina, Simona Lucibello, +37

Annals of Neurology

Diagnostic journey in Spinal Muscular Atrophy: Is it still an odyssey?

Maria Carmela Pera, Giorgia Coratti, Beatrice Berti, +15

PLoS ONE

Nusinersen efficacy data for 24‐month in type 2 and 3 spinal muscular atrophy

Marika Pane, Giorgia Coratti, Maria Carmela Pera, +24

Annals of Clinical and Translational Neurology

Respiratory Trajectories in Type 2 and 3 Spinal Muscular Atrophy in the iSMAC Cohort Study

Federica Trucco, Deborah Ridout, Mariacristina Scoto, +27

Neurology

Type I SMA “new natural history”: long‐term data in nusinersen‐treated patients

Marika Pane, Giorgia Coratti, Valeria Sansone, +23

Annals of Clinical and Translational Neurology

Revised North Star Ambulatory Assessment for Young Boys with Duchenne Muscular Dystrophy

Eugenio Mercuri, Giorgia Coratti, Sonia Messina, +16

PLoS ONE

Motor DevelopmentPediatric RehabilitationPediatric Orthopedic SurgeryKinesiologyAdolescent Medicine +20