Effectiveness of PTC124 treatment of cystic fibrosis caused by nonsense mutations: a prospective phase II trial

Eitan Kerem, Samit Hirawat, S. Armoni, +12

The Lancet

Ptc124 TreatmentMolecular Diagnostic TechniquesMendelian DisorderPathologyNonsense Mutations +2

Chronic ataluren (PTC124) treatment of nonsense mutation cystic fibrosis

Michael Wilschanski, L.L. Miller, David Shoseyov, +16

European Respiratory Journal

Evidence of Intestinal Inflammation in Patients With Cystic Fibrosis

Steven L. Werlin, Ishay Benuri‐Silbiger, Eitan Kerem, +13

Journal of Pediatric Gastroenterology and Nutrition

Intravenous monthly pulse methylprednisolone treatment for ABPA in patients with cystic fibrosis

Malena Cohen‐Cymberknoh, Hannah Blau, David Shoseyov, +4

Journal of Cystic Fibrosis

Pulmonary FibrosisMedicine

CFTR potentiator therapy ameliorates impaired insulin secretion in CF patients with a gating mutation

Reuven Tsabari, Hila Iron Elyashar, Malena Cohen Cymberknowh, +5

Journal of Cystic Fibrosis

Metabolic SyndromeCftr Potentiator TherapyMedicineInsulin ManagementDiabetes +7

18 F-Fluorodeoxyglucose-PET/CT Imaging of Lungs in Patients With Cystic Fibrosis

Martine Klein, Malena Cohen‐Cymberknoh, S. Armoni, +5

CHEST Journal

Positron Emission TomographyMedical ImagingAdvanced Lung DiseaseBiomedical ImagingPathology +5

Eradication failure of newly acquired Pseudomonas aeruginosa isolates in cystic fibrosis

Malena Cohen‐Cymberknoh, Noa Gilead, Silvia Gärtner, +15

Journal of Cystic Fibrosis

Eradication FailurePseudomonas Aeruginosa IsolatesAntibioticsKlebsiella PneumoniaeMicrobiology +4

Increasing Vitamin D Serum Levels Is Associated With Reduced Pulmonary Exacerbations in Patients With Cystic Fibrosis

Yasmeen Abu Fraiha, H. Elyashar-Earon, David Shoseyov, +4

Journal of Pediatric Gastroenterology and Nutrition

PTC124 treatment over 3 months improves pharmacodynamic and clinical parameters in patients with nonsense-mutation-mediated CF

M. Wilschanski, S. Armoni, Yasmin Yaakov, +8

Journal of Cystic Fibrosis

Gene TherapiesPtc124 TreatmentNonsense-mutation-mediated CfClinical TranslationGenetic Disorder +8

Intravenous methylprednisolone pulse therapy vs. oral prednisone for allergic bronchopulmonary aspergillosis (ABPA) in CF

Malena Cohen‐Cymberknoh, H. Blau, David Shoseyov, +3

Journal of Cystic Fibrosis

AsthmaAllergyAllergic Bronchopulmonary AspergillosisMedicineClinical Mycology +2