Christine Rivat

Molecular remission of infant B-ALL after infusion of universal TALEN gene-edited CAR T cells

Waseem Qasim, Hong Zhan, Sujith Samarasinghe et al. · Science Translational Medicine · 2017 · 871 citations

A Modified γ-Retrovirus Vector for X-Linked Severe Combined Immunodeficiency

Salima Hacein‐Bey‐Abina, Sung‐Yun Pai, H. Bobby Gaspar et al. · New England Journal of Medicine · 2014 · 402 citations · Full text

Outcomes Following Gene Therapy in Patients With Severe Wiskott-Aldrich Syndrome

Salima Hacein-Bey Abina, H. Bobby Gaspar, Johanna Blondeau et al. · JAMA · 2015 · 374 citations · Full text

Genome-edited, donor-derived allogeneic anti-CD19 chimeric antigen receptor T cells in paediatric and adult B-cell acute lymphoblastic leukaemia: results of two phase 1 studies

Reuben Benjamin, Charlotte Graham, Deborah Yallop et al. · The Lancet · 2020 · 344 citations · Full text

Hematological Malignancy, Cell Therapy, Transplantation +9

Lentiviral gene therapy for X-linked chronic granulomatous disease

Donald B. Kohn, Claire Booth, Elizabeth M. Kang et al. · Nature Medicine · 2020 · 242 citations · Full text

Primary Immunodeficiency, Autoimmune Disease, Lentiviral Gene Therapy +4