Waseem Qasim

Molecular remission of infant B-ALL after infusion of universal TALEN gene-edited CAR T cells

Waseem Qasim, Hong Zhan, Sujith Samarasinghe et al. · Science Translational Medicine · 2017 · 888 citations · Full text

Life Sciences, Immunology, Oncology +17

Comprehensive Rare Variant Analysis via Whole-Genome Sequencing to Determine the Molecular Pathology of Inherited Retinal Disease

Keren Carss, Gavin Arno, Marie Erwood et al. · The American Journal of Human Genetics · 2016 · 484 citations · Full text

Life Sciences, Genetics, Molecular Genetics +17

Base-Edited CAR7 T Cells for Relapsed T-Cell Acute Lymphoblastic Leukemia

Robert Chiesa, Christos Georgiadis, Farhatullah Syed et al. · New England Journal of Medicine · 2023 · 316 citations · Full text

Life Sciences, Molecular Biology, Oncology +16

Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: An international multicenter retrospective study

Federica Barzaghi, Bénédicte Neven, Silvia Ricci et al. · Journal of Allergy and Clinical Immunology · 2017 · 315 citations · Full text

Life Sciences, Hematology, Immunology +17

Long-term outcome and lineage-specific chimerism in 194 patients with Wiskott-Aldrich syndrome treated by hematopoietic cell transplantation in the period 1980-2009: an international collaborative study

Daniele Moratto, Silvia Giliani, Carmem Bonfim et al. · Blood · 2011 · 313 citations · Full text

Medicine, Hematology, Immunology +16