Identification of a myotropic AAV by massively parallel in vivo evaluation of barcoded capsid variants

Jonas Weinmann, Sabrina Weis, Josefine Sippel, +15

Nature Communications

Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells

Sumitava Dastidar, Simon Ardui, Kshitiz Singh, +20

Nucleic Acids Research

Nasopharyngeal Carcinoma Signaling Pathway: An Update on Molecular Biomarkers

Warut Tulalamba, Tavan Janvilisri

International Journal of Cell Biology

ImmunologyPathologyNasopharyngeal CarcinomaCancer BiologyTumor Biology +15

Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders

Jihad El Andari, Edith Renaud-Gabardos, Warut Tulalamba, +24

Science Advances

Therapeutic Gene DeliveryEngineeringIn Vivo Gene TherapySynthetic VirologyImmunology +20

A Novel Platform for Immune Tolerance Induction in Hemophilia A Mice

Simone Merlin, Elvira Stefania Cannizzo, Ester Borroni, +9

Molecular Therapy

Next-generation muscle-directed gene therapy by in silico vector design

Shilpita Sarcar, Warut Tulalamba, Melvin Y. Rincón, +16

Nature Communications

Prolactin alters the mRNA expression of osteoblast-derived osteoclastogenic factors in osteoblast-like UMR106 cells

Kannikar Wongdee, Warut Tulalamba, Jirawan Thongbunchoo, +2

Molecular and Cellular Biochemistry

Mrna ExpressionSclerostinDevelopmental BiologyBone Morphogenic ProteinOsteoblast-derived Osteoclastogenic Factors +7

Distinct transduction of muscle tissue in mice after systemic delivery of AAVpo1 vectors

Warut Tulalamba, Jonas Weinmann, Quang Hong Pham, +4

Gene Therapy

Regenerative MedicineMuscle TissueDistinct TransductionAavpo1 VectorsViral Pathogenesis +6

Treatment of infantile-onset Pompe disease in a rat model with muscle-directed AAV gene therapy

Sergio Muñoz, Joan Bertolin, Verónica Jiménez, +16

Molecular Metabolism

Validation of miR-20a as a Tumor Suppressor Gene in Liver Carcinoma Using Hepatocyte-Specific Hyperactive piggyBac Transposons

Jaitip Tipanee, Mario Di Matteo, Warut Tulalamba, +5

Molecular Therapy — Nucleic Acids