Ellyn L. Peterson

Systemic Delivery of Dysferlin Overlap Vectors Provides Long-Term Gene Expression and Functional Improvement for Dysferlinopathy

Rachael A. Potter, Danielle A. Griffin, Patricia Sondergaard et al. · Human Gene Therapy · 2017 · 86 citations · Full text

Medicine, Molecular Biology, Molecular Medicine +16

Dose-Escalation Study of Systemically Delivered rAAVrh74.MHCK7.micro-dystrophin in the <i>mdx</i> Mouse Model of Duchenne Muscular Dystrophy

Rachael A. Potter, Danielle A. Griffin, Kristin N. Heller et al. · Human Gene Therapy · 2021 · 85 citations · Full text

Medicine, Molecular Biology, Molecular Genetics +17

Gene Delivery for Limb-Girdle Muscular Dystrophy Type 2D by Isolated Limb Infusion

Jerry R. Mendell, Louis G. Chicoine, Samiah Al-Zaidy et al. · Human Gene Therapy · 2019 · 45 citations · Full text

Life Sciences, Biotechnology, Genetics +17

Use of plasmapheresis to lower anti-AAV antibodies in nonhuman primates with pre-existing immunity to AAVrh74

Rachael A. Potter, Ellyn L. Peterson, Danielle Griffin et al. · Molecular Therapy — Methods & Clinical Development · 2024 · 31 citations · Full text

Medicine, Immunology, Pharmacology +15

Preclinical Systemic Delivery of Adeno-Associated α-Sarcoglycan Gene Transfer for Limb-Girdle Muscular Dystrophy

Danielle A. Griffin, Eric R. Pozsgai, Kristin N. Heller et al. · Human Gene Therapy · 2020 · 22 citations · Full text

Medicine, Molecular Biology, Molecular Genetics +14