Danielle A. Griffin

Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy

Jerry R. Mendell, Zarife Sahenk, Kelly J. Lehman et al. · JAMA Neurology · 2020 · 360 citations · Full text

Defective membrane fusion and repair in<i>Anoctamin5</i>-deficient muscular dystrophy

Danielle A. Griffin, R.W. Johnson, Jarred M. Whitlock et al. · Human Molecular Genetics · 2016 · 107 citations · Full text

Engineering, Molecular Biology, Cytoskeleton +18

AAV.Dysferlin Overlap Vectors Restore Function in Dysferlinopathy Animal Models

Patricia Sondergaard, Danielle A. Griffin, Eric R. Pozsgai et al. · Annals of Clinical and Translational Neurology · 2015 · 95 citations · Full text

Systemic Delivery of Dysferlin Overlap Vectors Provides Long-Term Gene Expression and Functional Improvement for Dysferlinopathy

Rachael A. Potter, Danielle A. Griffin, Patricia Sondergaard et al. · Human Gene Therapy · 2017 · 85 citations · Full text

Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged ≥4 to &lt;8 Years) with Duchenne Muscular Dystrophy: 1‐Year Interim Results from Study <scp>SRP</scp>‐9001‐103 (<scp>ENDEAVOR</scp>)

Craig M. Zaidman, Crystal M. Proud, Craig M. McDonald et al. · Annals of Neurology · 2023 · 83 citations · Full text