Megha Nivsarkar

In utero gene transfer of human factor IX to fetal mice can induce postnatal tolerance of the exogenous clotting factor

Simon N. Waddington, Suzanne M. K. Buckley, Megha Nivsarkar et al. · Blood · 2003 · 112 citations · Full text

Life Sciences, Developmental Biology, Genetics +16

Long-term transgene expression by administration of a lentivirus-based vector to the fetal circulation of immuno-competent mice

Simon N. Waddington, Kyriacos Mitrophanous, Fiona M. Ellard et al. · Gene Therapy · 2003 · 79 citations · Full text

Life Sciences, Molecular Biology, Molecular Genetics +17

Ultrasound-Guided Percutaneous Delivery of Adenoviral Vectors Encoding the <i>β</i> -Galactosidase and Human Factor IX Genes to Early Gestation Fetal Sheep <i>In Utero</i>

Anna L. David, Terry Cook, Simon N. Waddington et al. · Human Gene Therapy · 2003 · 65 citations

Medicine, Genetics, Obstetrics +17

Widespread and efficient marker gene expression in the airway epithelia of fetal sheep after minimally invasive tracheal application of recombinant adenovirus in utero

Donald Peebles, L. Gregory, Anna L. David et al. · Gene Therapy · 2003 · 62 citations

Life Sciences, Developmental Biology, Molecular Biology +17

Permanent partial phenotypic correction and tolerance in a mouse model of hemophilia B by stem cell gene delivery of human factor IX

Brian Bigger, Elena K. Siapati, Ajay Mistry et al. · Gene Therapy · 2005 · 49 citations

Medicine, Hematology, Molecular Biology +16