Steven G. Hughes

Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis

Merrill D. Benson, Márcia Waddington‐Cruz, John L. Berk et al. · New England Journal of Medicine · 2018 · 1.4K citations · Full text

Life Sciences, Pharmacology, Pharmacotherapy +16

A consensus protocol for the standardization of cerebrospinal fluid collection and biobanking

Charlotte E. Teunissen, Axel Petzold, Jeffrey L. Bennett et al. · Neurology · 2009 · 856 citations · Full text

Life Sciences, Neurology, Neuroscience +14

Antisense oligonucleotides targeting apolipoprotein(a) in people with raised lipoprotein(a): two randomised, double-blind, placebo-controlled, dose-ranging trials

Nicholas J. Viney, Julian C. van Capelleveen, Richard S. Geary et al. · The Lancet · 2016 · 748 citations

Medicine, Pharmacology, Clinical Pharmacology +6

Volanesorsen and Triglyceride Levels in Familial Chylomicronemia Syndrome

Joseph L. Witztum, Daniel Gaudet, Steven D. Freedman et al. · New England Journal of Medicine · 2019 · 669 citations · Full text

Life Sciences, Biochemistry, Pharmacology +17

Cardiovascular and Metabolic Effects of <i>ANGPTL3</i> Antisense Oligonucleotides

Mark J. Graham, Richard Lee, Teresa Brandt et al. · New England Journal of Medicine · 2017 · 581 citations · Full text

Medicine, Pharmacokinetics, Pharmacology +14