Catherine McGuinn

Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant

Lindsey A. George, Spencer K. Sullivan, Adam Giermasz et al. · New England Journal of Medicine · 2017 · 759 citations · Full text

Medicine, Hematology, Molecular Medicine +15

Congenital fibrinogen disorders: a retrospective clinical and genetic analysis of the Prospective Rare Bleeding Disorders Database

Samin Mohsenian, Roberta Palla, Marzia Menegatti et al. · Blood Advances · 2024 · 44 citations · Full text

Medicine, Genetics, Molecular Genetics +17

Diagnostic work‐up for severe aplastic anemia in children: Consensus of the <scp>North American Pediatric Aplastic Anemia Consortium</scp>

Kristin A. Shimano, Anupama Narla, Melissa J. Rose et al. · American Journal of Hematology · 2021 · 38 citations · Full text

Medicine, Hematology, Pediatrics +17

Efficacy and Safety in 15 Hemophilia B Patients Treated with the AAV Gene Therapy Vector Fidanacogene Elaparvovec and Followed for at Least 1 Year

Lindsey A. George, Spencer K. Sullivan, John E.J. Rasko et al. · Blood · 2019 · 37 citations

Medicine, Hematology, Molecular Medicine +10

The prospective Hemophilia Inhibitor PUP Study reveals distinct antibody signatures prior to FVIII inhibitor development

Birgit M. Reipert, Bagirath Gangadharan, Christoph J. Hofbauer et al. · Blood Advances · 2020 · 35 citations · Full text

Medicine, Hematology, Immunology +13