Clinical spectrum of pyruvate kinase deficiency: data from the Pyruvate Kinase Deficiency Natural History Study

Rachael F. Grace, Paola Bianchi, Eduard J. van Beers, +37

Blood

Romiplostim in children with immune thrombocytopenia: a phase 3, randomised, double-blind, placebo-controlled study

Michael D. Tarantino, James B. Bussel, Victor S. Blanchette, +10

The Lancet

ThrombopoiesisThrombosisBone Marrow FailureAutoimmune DiseaseBlood Platelet +9

Monogenic early-onset lymphoproliferation and autoimmunity: Natural history of STAT3 gain-of-function syndrome

Jennifer W. Leiding, Tiphanie P. Vogel, Valentine G.J. Santarlas, +97

Journal of Allergy and Clinical Immunology

Stat3 Gain-of-function SyndromeMonogenic Early-onset LymphoproliferationAutoimmune DiseaseAutoantibody ProductionImmune Cell Development +11

Second‐line treatments in children with immune thrombocytopenia: Effect on platelet count and patient‐centered outcomes

Rachael F. Grace, Kristin A. Shimano, Rukhmi Bhat, +21

American Journal of Hematology

Isolated ThrombocytopeniaImmunologyPharmacotherapyKids Itp ToolImmunotherapy +16

Physician decision making in selection of second‐line treatments in immune thrombocytopenia in children

Rachael F. Grace, Jenny M. Despotovic, Carolyn M. Bennett, +21

American Journal of Hematology

Patient SelectionChronic ItpThrombosisPrimary CareVenous Thrombosis +15

Outcomes of Hematopoietic Cell Transplantation in Patients with Germline SAMD9/SAMD9L Mutations

Ibrahim Ahmed, Midhat S. Farooqi, Mark T. Vander Lugt, +9

Biology of Blood and Marrow Transplantation

GeneticsImmunodeficienciesGenetic EpidemiologyImmunologyPathology +23

Diagnosis and Reconstruction of the Human Temporomandibular Joint after Trauma or Internal Derangement

Russell W. Bessette, Richard W. Katzberg, Joseph R. Natiella, +1

Plastic & Reconstructive Surgery

Internal DerangementSurgeryOrthopaedic SurgeryFacial TraumaStandardized Records +18

Congenital amegakaryocytic thrombocytopenia: The diagnostic importance of combining pathology with molecular genetics

Melissa J. Rose, Kathleen Nicol, Micah Skeens, +2

Pediatric Blood & Cancer

Diagnostic work‐up for severe aplastic anemia in children: Consensus of the <scp>North American Pediatric Aplastic Anemia Consortium</scp>

Kristin A. Shimano, Anupama Narla, Melissa J. Rose, +23

American Journal of Hematology

DiagnosisAplastic AnemiaHospital MedicineBone Marrow FailureLaboratory Hematology +14

Patterns of Inpatient Care for Newly Diagnosed Immune Thrombocytopenia in US Children’s Hospitals

Courtney Kime, Jennifer Klima, Melissa J. Rose, +1

PEDIATRICS