Thomas W. Ferkol

Mutational Analysis of the Adeno-Associated Virus Type 2 (AAV2) Capsid Gene and Construction of AAV2 Vectors with Altered Tropism

Pei Wu, Wu Xiao, Thomas J. Conlon et al. · Journal of Virology · 2000 · 381 citations · Full text

Gene transfer in vivo: sustained expression and regulation of genes introduced into the liver by receptor-targeted uptake.

José C. Perales, Thomas W. Ferkol, H. Beegen et al. · Proceedings of the National Academy of Sciences · 1994 · 303 citations · Full text

Molecular Biology, Gene Delivery, Receptor-targeted Uptake +19

Repeated Aerosolized AAV-CFTR for Treatment of Cystic Fibrosis: A Randomized Placebo-Controlled Phase 2B Trial

Richard B. Moss, Carlos Milla, John L. Colombo et al. · Human Gene Therapy · 2007 · 267 citations

Standardizing Nasal Nitric Oxide Measurement as a Test for Primary Ciliary Dyskinesia

Margaret W. Leigh, Milan J. Hazucha, Kunal Chawla et al. · Annals of the American Thoracic Society · 2013 · 264 citations · Full text

Clinical Features of Childhood Primary Ciliary Dyskinesia by Genotype and Ultrastructural Phenotype

Stephanie D. Davis, Thomas W. Ferkol, Margaret Rosenfeld et al. · American Journal of Respiratory and Critical Care Medicine · 2014 · 261 citations · Full text