Nora Watman

A reappraisal of Gaucher disease—diagnosis and disease management algorithms

Pramod K. Mistry, Maria Domenica Cappellini, Elena Lukina et al. · American Journal of Hematology · 2010 · 188 citations · Full text

Life Sciences, Neurology, Pathology +17

Improvement in hematological, visceral, and skeletal manifestations of Gaucher disease type 1 with oral eliglustat tartrate (Genz-112638) treatment: 2-year results of a phase 2 study

Elena Lukina, Nora Watman, Elsa Ávila Arreguin et al. · Blood · 2010 · 157 citations · Full text

Medicine, Hematology, Pharmacotherapy +3

A phase 2 study of eliglustat tartrate (Genz-112638), an oral substrate reduction therapy for Gaucher disease type 1

Elena Lukina, Nora Watman, Elsa Ávila Arreguin et al. · Blood · 2010 · 154 citations · Full text

Pharmacy, Pharmacotherapy, Oral Drug Delivery +3

Prospective evaluation of patient-reported outcomes during treatment with deferasirox or deferoxamine for iron overload in patients with β-thalassemia

Maria Domenica Cappellini, Mohamed Béjaoui, Leyla Ağaoğlu et al. · Clinical Therapeutics · 2007 · 118 citations

Medicine, Hematology, Pharmacotherapy +14

Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy

Timothy M. Cox, Guillermo Drelichman, Renata Cravo et al. · Blood · 2017 · 92 citations · Full text

Life Sciences, Internal Medicine, Pharmacotherapy +9