Leonard O. Marque

Nuclear retention of full-length HTT RNA is mediated by splicing factors MBNL1 and U2AF65

Xin Sun, Pan P. Li, Shanshan Zhu et al. · Scientific Reports · 2015 · 55 citations · Full text

Life Sciences, Genetics, Molecular Genetics +17

Phosphorodiamidate morpholino oligomers suppress mutant huntingtin expression and attenuate neurotoxicity

Xin Sun, Leonard O. Marque, Zachary A. Cordner et al. · Human Molecular Genetics · 2014 · 39 citations · Full text

Life Sciences, Genetics, Molecular Biology +17

<scp>RNA</scp> Toxicity and Perturbation of <scp>rRNA</scp> Processing in Spinocerebellar Ataxia Type <scp>2</scp>

Pan P. Li, Roumita Moulick, Hongxuan Feng et al. · Movement Disorders · 2021 · 21 citations · Full text

Life Sciences, Molecular Biology, Neuroscience +17

Immortalized striatal precursor neurons from Huntington’s disease patient-derived iPS cells as a platform for target identification and screening for experimental therapeutics

Sergey Akimov, Mali Jiang, Amanda J. Kedaigle et al. · Human Molecular Genetics · 2021 · 18 citations · Full text

Life Sciences, Neurobiology, Neuroscience +17