Alexander Sumaroka

Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics

Artur V. Cideciyan, Tomás S. Alemán, Sanford L. Boye et al. · Proceedings of the National Academy of Sciences · 2008 · 664 citations · Full text

Medicine, Genetics, Ophthalmology +17

Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement

Artur V. Cideciyan, Samuel G. Jacobson, William A. Beltran et al. · Proceedings of the National Academy of Sciences · 2013 · 440 citations · Full text

Medicine, Ophthalmology, Vision Science +17

Improvement and Decline in Vision with Gene Therapy in Childhood Blindness

Samuel G. Jacobson, Artur V. Cideciyan, Alejandro J. Román et al. · New England Journal of Medicine · 2015 · 377 citations · Full text

Medicine, Ophthalmology, Vision Science +17

Human <i>RPE65</i> Gene Therapy for Leber Congenital Amaurosis: Persistence of Early Visual Improvements and Safety at 1 Year

Artur V. Cideciyan, William W. Hauswirth, Tomás S. Alemán et al. · Human Gene Therapy · 2009 · 312 citations · Full text

Medicine, Immunology, Ophthalmology +17

Probing Mechanisms of Photoreceptor Degeneration in a New Mouse Model of the Common Form of Autosomal Dominant Retinitis Pigmentosa due to P23H Opsin Mutations

Sanae Sakami, Tadao Maeda, Grzegorz Bereta et al. · Journal of Biological Chemistry · 2011 · 304 citations · Full text

Medicine, Genetics, Ophthalmology +17