Concepedia

Author

Pauline Sellier

Inserm

Also Known As

P. Sellier, Pauline Sellier

18

Publications

367

Citations

9

H-Index

5

Concepts

All Affiliations

InsermGenethon (France)Sorbonne UniversitéUniversité Paris-SaclaySpark Therapeutics (United States)
PS

About

Pauline Sellier is an author at Inserm specializing in gene therapies, immunology, and viral immunity.

Top Concepts

#ConceptH-IndexPublicationsCitations

1

Medicine

1

1

70

2

Immunology

1

1

70

3

Gene Therapies

1

1

70

4

Viral Immunity

1

1

70

5

Gene Transfer

1

1

70

Pauline Sellier

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9

Publications

354

Citations

9

H-Index

YearCitations

Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase

Francesco Puzzo, Pasqualina Colella, Maria Grazia Biferi,

Science Translational Medicine

2017

129

AAV Gene Transfer with Tandem Promoter Design Prevents Anti-transgene Immunity and Provides Persistent Efficacy in Neonate Pompe Mice

Pasqualina Colella, Pauline Sellier, Helena Costa Verdera,

Molecular Therapy — Methods & Clinical Development

2018

70

Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates

Helena Costa Verdera, Fanny Collaud, Christopher Riling,

Nature Communications

2021

36

Gene therapy with secreted acid alpha-glucosidase rescues Pompe disease in a novel mouse model with early-onset spinal cord and respiratory defects

Pasqualina Colella, Pauline Sellier, Manuel J. Gómez,

EBioMedicine

2020

27

Kininogen Cleavage Assay: Diagnostic Assistance for Kinin-Mediated Angioedema Conditions

Rémi Baroso, Pauline Sellier, Federica Defendi,

PLoS ONE

2016

23

Rescue of Advanced Pompe Disease in Mice with Hepatic Expression of Secretable Acid α-Glucosidase

Umut Cagin, Francesco Puzzo, Manuel J. Gómez,

Molecular Therapy

2020

22

C1 inhibitor function using contact‐phase proteases as target: evaluation of an innovative assay

Arije Ghannam, Pauline Sellier, Federica Defendi,

Allergy

2015

21

Muscle‐specific, liver‐detargeted <scp>adeno‐associated virus</scp> gene therapy rescues Pompe phenotype in adult and neonate <scp><i>Gaa</i><sup>−/−</sup></scp> mice

Pauline Sellier, Pierre Vidal, Benjamin Bertin,

Journal of Inherited Metabolic Disease

2023

16

C1 Inhibitor as a glycoprotein: The influence of polysaccharides on its function and autoantibody target

Arije Ghannam, Pauline Sellier, O. Fain,

Molecular Immunology

2016

10

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