Julián Sevilla

Emapalumab in Children with Primary Hemophagocytic Lymphohistiocytosis

Franco Locatelli, Michael B. Jordan, Carl E. Allen et al. · New England Journal of Medicine · 2020 · 511 citations · Full text

Medicine, Hematology, Pediatrics +14

Eltrombopag for the treatment of children with persistent and chronic immune thrombocytopenia (PETIT): a randomised, multicentre, placebo-controlled study

James B. Bussel, Purificación García de Miguel, Jenny M. Despotovic et al. · The Lancet Haematology · 2015 · 195 citations

Medicine, Pediatrics, Pharmacology +8

Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia

Susana Navarro, Wei Wang, Rebeca Sánchez‐Domínguez et al. · Nature Medicine · 2019 · 176 citations

Medicine, Cell Biology, Hematology +17

Dabigatran etexilate for the treatment of acute venous thromboembolism in children (DIVERSITY): a randomised, controlled, open-label, phase 2b/3, non-inferiority trial

Leonardo R. Brandão, Matteo Luciani, Lisa Bomgaars et al. · The Lancet Haematology · 2020 · 149 citations · Full text

Medicine, Pediatrics, Pharmacotherapy +12

Chromosome fragility in patients with Fanconi anaemia: diagnostic implications and clinical impact

M.J. Ramírez, José Antonio Casado, María Talavera et al. · Journal of Medical Genetics · 2011 · 144 citations · Full text

Life Sciences, Genetics, Hematology +17