Karen Walton–Bowen

Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human α-L-iduronidase (laronidase)

J. E. Wraith, L. Clarke, Michael Beck et al. · The Journal of Pediatrics · 2004 · 546 citations

Life Sciences, Biochemistry, Enzymology +7

Effects of STX209 (Arbaclofen) on Neurobehavioral Function in Children and Adults with Fragile X Syndrome: A Randomized, Controlled, Phase 2 Trial

Elizabeth Berry‐Kravis, David Hessl, Barbara Rathmell et al. · Science Translational Medicine · 2012 · 325 citations · Full text

Medicine, Neuroscience, Pharmacotherapy +17

A Multiple-dosing, Placebo-controlled Study of Budesonide Inhalation Suspension Given Once or Twice Daily for Treatment of Persistent Asthma in Young Children and Infants

James Baker, Michael Mellon, Jeffrey Wald et al. · PEDIATRICS · 1999 · 200 citations

Pharmacy, Pediatrics, Pharmacology +17

Arbaclofen in fragile X syndrome: results of phase 3 trials

Elizabeth Berry‐Kravis, Randi J. Hagerman, Jeannie Visootsak et al. · Journal of Neurodevelopmental Disorders · 2017 · 184 citations · Full text

Medicine, Pharmacotherapy, Psychiatry +16

Budesonide enema for the treatment of active, distal ulcerative colitis and proctitis: A dose-ranging study

Stephen B. Hanauer, Malcolm Robinson, Ronald E. Pruitt et al. · Gastroenterology · 1998 · 177 citations · Full text

Nursing, Internal Medicine, Pharmacotherapy +16