Tiwaporn Nualkaew

SLN124, a GalNac‐siRNA targeting transmembrane serine protease 6, in combination with deferiprone therapy reduces ineffective erythropoiesis and hepatic iron‐overload in a mouse model of β‐thalassaemia

Jim Vadolas, Garrett Z. Ng, Kai Kysenius et al. · British Journal of Haematology · 2021 · 30 citations · Full text

Medicine, Hematology, Molecular Biology +17

UNC0638 induces high levels of fetal hemoglobin expression in β-thalassemia/HbE erythroid progenitor cells

Tiwaporn Nualkaew, Pinyaphat Khamphikham, Phitchapa Pongpaksupasin et al. · Annals of Hematology · 2020 · 23 citations

Life Sciences, Genetics, Molecular Genetics +12

Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia

Tiwaporn Nualkaew, Karine Sii-Felice, Marie Giorgi et al. · Molecular Therapy · 2021 · 17 citations · Full text

Life Sciences, Molecular Biology, Molecular Genetics +17

Enhancement of β-Globin Gene Expression in Thalassemic IVS2-654 Induced Pluripotent Stem Cell-Derived Erythroid Cells by Modified U7 snRNA

Phetcharat Phanthong, Suparerk Borwornpinyo, Narisorn Kitiyanant et al. · Stem Cells Translational Medicine · 2017 · 14 citations · Full text

Life Sciences, Genetics, Hematology +17

Engineered U7 snRNA mediates sustained splicing correction in erythroid cells from β-thalassemia/HbE patients

Sarinthip Preedagasamzin, Tiwaporn Nualkaew, Tanjitti Pongrujikorn et al. · Biochemical and Biophysical Research Communications · 2018 · 12 citations

Life Sciences, Genetics, Molecular Biology +12