Concepedia

UNC0638 induces high levels of fetal hemoglobin expression in β-thalassemia/HbE erythroid progenitor cells

Tiwaporn Nualkaew, Pinyaphat Khamphikham, Phitchapa Pongpaksupasin, Woratree Kaewsakulthong, Duantida Songdej, Kittiphong Paiboonsukwong, Orapan Sripichai, James Douglas Engel, Suradej Hongeng, Suthat Fucharoen,

Annals of Hematology · 2020 · 23 citations · 33 references

DOI

Concepts

References

33

Effect of Hydroxyurea on the Frequency of Painful Crises in Sickle Cell Anemia

Samuel Charache, Michael L. Terrin, Richard D. Moore et al. · New England Journal of Medicine · 1995 · 2.3K citations · Full text

, , +9

Genome-wide association study shows <i>BCL11A</i> associated with persistent fetal hemoglobin and amelioration of the phenotype of β-thalassemia

Manuela Uda, Renzo Galanello, Serena Sanna et al. · Proceedings of the National Academy of Sciences · 2008 · 672 citations · Full text

, , +17

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Alexis A. Thompson, Mark C. Walters, Janet L. Kwiatkowski et al. · New England Journal of Medicine · 2018 · 661 citations · Full text

, , +16

A Phase 3 Trial of <scp>l</scp> -Glutamine in Sickle Cell Disease

Yutaka Niihara, Scott T. Miller, Julie Kanter et al. · New England Journal of Medicine · 2018 · 546 citations · Full text

, , +8

The effect of prolonged administration of hydroxyurea on morbidity and mortality in adult patients with sickle cell syndromes: results of a 17-year, single-center trial (LaSHS)

Ersi Voskaridou, Dimitrios Christoulas, Antonios Bilalis et al. · Blood · 2009 · 432 citations · Full text

, , +5