Natalie L. Goedeker

Thrombotic Microangiopathy Following Onasemnogene Abeparvovec for Spinal Muscular Atrophy: A Case Series

Deepa H. Chand, Craig M. Zaidman, Kapil Arya et al. · The Journal of Pediatrics · 2020 · 186 citations · Full text

Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged ≥4 to &lt;8 Years) with Duchenne Muscular Dystrophy: 1‐Year Interim Results from Study <scp>SRP</scp>‐9001‐103 (<scp>ENDEAVOR</scp>)

Craig M. Zaidman, Crystal M. Proud, Craig M. McDonald et al. · Annals of Neurology · 2023 · 83 citations · Full text

Evaluation of rAAVrh74 gene therapy vector seroprevalence by measurement of total binding antibodies in patients with Duchenne muscular dystrophy

Natalie L. Goedeker, Sachi D. Dharia, Danielle A. Griffin et al. · Therapeutic Advances in Neurological Disorders · 2023 · 43 citations · Full text

Laboratory monitoring of nusinersen safety

Natalie L. Goedeker, Jennifer L. Gibbons, Arun S. Varadhachary et al. · Muscle & Nerve · 2021 · 18 citations

Management of Select Adverse Events Following Delandistrogene Moxeparvovec Gene Therapy for Patients With Duchenne Muscular Dystrophy

Craig M. Zaidman, Natalie L. Goedeker, Amal Aqul et al. · Journal of Neuromuscular Diseases · 2024 · 16 citations · Full text