Raisa Jofra Hernández

Alterations in the adenosine metabolism and CD39/CD73 adenosinergic machinery cause loss of Treg cell function and autoimmunity in ADA-deficient SCID

Aisha V. Sauer, Immacolata Brigida, Nicola Carriglio et al. · Blood · 2011 · 104 citations · Full text

Ex vivo gene therapy with lentiviral vectors rescues adenosine deaminase (ADA)–deficient mice and corrects their immune and metabolic defects

Alessandra Mortellaro, Raisa Jofra Hernández, Matteo M. Guerrini et al. · Blood · 2006 · 77 citations · Full text

Efficacy of Gene Therapy for Wiskott-Aldrich Syndrome Using a WAS Promoter/cDNA-Containing Lentiviral Vector and Nonlethal Irradiation

Francesco Marangoni, Samantha Scaramuzza, Sara Trifari et al. · Human Gene Therapy · 2006 · 77 citations

Preclinical Safety and Efficacy of Human CD34+ Cells Transduced With Lentiviral Vector for the Treatment of Wiskott-Aldrich Syndrome

Samantha Scaramuzza, Luca Biasco, Anna Ripamonti et al. · Molecular Therapy · 2012 · 76 citations · Full text

ADA-deficient SCID is associated with a specific microenvironment and bone phenotype characterized by RANKL/OPG imbalance and osteoblast insufficiency

Aisha V. Sauer, Emanuela Mrak, Raisa Jofra Hernández et al. · Blood · 2009 · 75 citations