Francisco J Roman‐Rodriguez

Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia

Susana Navarro, Wei Wang, Rebeca Sánchez‐Domínguez et al. · Nature Medicine · 2019 · 170 citations

Fanconi Anemia, Cell Therapy, Non-conditioned Patients +11

NHEJ-Mediated Repair of CRISPR-Cas9-Induced DNA Breaks Efficiently Corrects Mutations in HSPCs from Patients with Fanconi Anemia

Francisco J Roman‐Rodriguez, Laura Ugalde, Lara Álvarez et al. · Cell stem cell · 2019 · 85 citations · Full text

Fanconi Anemia, Genome Instability, Genetics +8

Therapeutic gene editing in <scp>CD</scp> 34 ⁺ hematopoietic progenitors from Fanconi anemia patients

Begoña Díez, Pietro Genovese, Francisco J Roman‐Rodriguez et al. · EMBO Molecular Medicine · 2017 · 58 citations · Full text

Measles virus envelope pseudotyped lentiviral vectors transduce quiescent human HSCs at an efficiency without precedent

Camille Lévy, Fouzia Amirache, Anais Girard-Gagnepain et al. · Blood Advances · 2017 · 47 citations · Full text

Involvement of DNMT3B in the pathogenesis of Hirschsprung disease and its possible role as a regulator of neurogenesis in the human enteric nervous system

Ana Torroglosa, María Valle Enguix-Riego, Raquel M. Fernández et al. · Genetics in Medicine · 2014 · 30 citations · Full text

Molecular Neuroscience, Developmental Biology, Autophagy +9