Jeffrey Rothstein

An antisense oligonucleotide against SOD1 delivered intrathecally for patients with SOD1 familial amyotrophic lateral sclerosis: a phase 1, randomised, first-in-man study

Timothy M. Miller, Alan Pestronk, William David et al. · The Lancet Neurology · 2013 · 607 citations · Full text

Medicine, Neurology, Pharmacology +17

Identification of active loci of a human endogenous retrovirus in neurons of patients with amyotrophic lateral sclerosis

Renée N. Douville, Jiankai Liu, Jeffrey Rothstein et al. · Annals of Neurology · 2010 · 324 citations

Life Sciences, Neurology, Neuroscience +13

Optimizing Nervous System-Specific Gene Targeting with Cre Driver Lines: Prevalence of Germline Recombination and Influencing Factors

Lin Luo, Mateusz C. Ambrozkiewicz, Fritz Benseler et al. · Neuron · 2020 · 196 citations · Full text

Life Sciences, Genetics, Molecular Genetics +16

Concordant but Varied Phenotypes among Duchenne Muscular Dystrophy Patient-Specific Myoblasts Derived using a Human iPSC-Based Model

In Young Choi, Hotae Lim, Kenneth Estrellas et al. · Cell Reports · 2016 · 184 citations · Full text

Life Sciences, Biotechnology, Genetics +17

MC-100093, a Novel β-Lactam Glutamate Transporter-1 Enhancer Devoid of Antimicrobial Properties, Attenuates Cocaine Relapse in Rats

Lori A. Knackstedt, Lizhen Wu, Jeffrey Rothstein et al. · Journal of Pharmacology and Experimental Therapeutics · 2021 · 20 citations · Full text

Medicine, Neuroscience, Pharmacology +17