Guillaume Tanniou

Gene therapy with secreted acid alpha-glucosidase rescues Pompe disease in a novel mouse model with early-onset spinal cord and respiratory defects

Pasqualina Colella, Pauline Sellier, Manuel J. Gómez et al. · EBioMedicine · 2020 · 27 citations · Full text

Medicine, Molecular Biology, Molecular Genetics +14

Pre-clinical study of 21 approved drugs in the mdx mouse

Maïté Carre-Pierrat, Aude Lafoux, Guillaume Tanniou et al. · Neuromuscular Disorders · 2011 · 23 citations

Veterinary Medicine, Pharmacokinetics, Pharmacology +8

Co-Administration of Simvastatin Does Not Potentiate the Benefit of Gene Therapy in the mdx Mouse Model for Duchenne Muscular Dystrophy

Nathalie Bourg, Ai Vu Hong, William Lostal et al. · International Journal of Molecular Sciences · 2022 · 14 citations · Full text

Medicine, Pharmacology, Pharmacotherapy +15