Maria Candida Vila

Effect of genetic background on the dystrophic phenotype in<i>mdx</i>mice

William Coley, Laurent Bogdanik, Maria Candida Vila et al. · Human Molecular Genetics · 2015 · 252 citations · Full text

Life Sciences, Genetics, Molecular Genetics +15

Mitochondria mediate cell membrane repair and contribute to Duchenne muscular dystrophy

Maria Candida Vila, Sree Rayavarapu, Marshall W. Hogarth et al. · Cell Death and Differentiation · 2016 · 145 citations · Full text

Life Sciences, Cell Biology, Genetics +16

Cell-Selective Adeno-Associated Virus-Mediated <i>SCN1A</i> Gene Regulation Therapy Rescues Mortality and Seizure Phenotypes in a Dravet Syndrome Mouse Model and Is Well Tolerated in Nonhuman Primates

Annie Tanenhaus, T. D. Stowe, Andrew L. Young et al. · Human Gene Therapy · 2022 · 121 citations · Full text

Life Sciences, Neurology, Neuroscience +17

Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy

Yusuke Echigoya, Kenji Rowel Q. Lim, Nhu Trieu et al. · Molecular Therapy · 2017 · 87 citations · Full text

Medicine, Molecular Genetics, Molecular Medicine +5

TNF-α-Induced microRNAs Control Dystrophin Expression in Becker Muscular Dystrophy

Alyson A. Fiorillo, Christopher R. Heier, James S. Novak et al. · Cell Reports · 2015 · 84 citations · Full text

Life Sciences, Immunology, Molecular Biology +16