Jade Samulski

Dystrophin Immunity in Duchenne's Muscular Dystrophy

Jerry R. Mendell, Katherine Campbell, Louise R. Rodino‐Klapac et al. · New England Journal of Medicine · 2010 · 655 citations · Full text

Medicine, Immunology, Molecular Genetics +15

Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

Dawn E. Bowles, Scott McPhee, Chengwen Li et al. · Molecular Therapy · 2011 · 392 citations · Full text

Pharmacy, Biotechnology, Immunology +16

Employing a Gain-of-Function Factor IX Variant R338L to Advance the Efficacy and Safety of Hemophilia B Human Gene Therapy: Preclinical Evaluation Supporting an Ongoing Adeno-Associated Virus Clinical Trial

Paul E. Monahan, Junjiang Sun, Tong Gui et al. · Human Gene Therapy · 2014 · 107 citations · Full text

Medicine, Hematology, Molecular Medicine +13

Cardiac I-1c Overexpression With Reengineered AAV Improves Cardiac Function in Swine Ischemic Heart Failure

Kiyotake Ishikawa, Kenneth Fish, Lisa Tilemann et al. · Molecular Therapy · 2014 · 85 citations · Full text

Medicine, Cardiology, Molecular Biology +13

Self-complementary AAV2.5-BMP2-coated Femoral Allografts Mediated Superior Bone Healing Versus Live Autografts in Mice With Equivalent Biomechanics to Unfractured Femur

Masahiko Takahata, David G. Reynolds, Chao Xie et al. · Molecular Therapy · 2011 · 57 citations · Full text

Medicine, Orthopaedic Surgery, Orthopedic Surgery +17