Concepedia

Pablo Morales

PM

11

Publications

1.5K

Citations

10

H-Index

2007

Active since

Affiliations

Nationwide Children's Hospital(Current)

The Ohio State University

Emory University

Roche (United States)

Pablo Morales is an author at Nationwide Children's Hospital specializing in medicine, physiology, and neuroregeneration.

ORCID

Top concepts

Publications per year

2007–2023

11

Publications

11

RETRACTED ARTICLE: Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN

Kevin D. Foust, Xueyong Wang, Vicki L. McGovern et al. · Nature Biotechnology · 2010 · 685 citations · Full text

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Systemic Gene Delivery in Large Species for Targeting Spinal Cord, Brain, and Peripheral Tissues for Pediatric Disorders

Adam K. Bevan, Sandra Duqué, Kevin D. Foust et al. · Molecular Therapy · 2011 · 327 citations · Full text

Improving Single Injection CSF Delivery of AAV9-mediated Gene Therapy for SMA: A Dose–response Study in Mice and Nonhuman Primates

Kathrin Meyer, Laura Ferraiuolo, Leah Schmelzer et al. · Molecular Therapy · 2014 · 269 citations · Full text

A BMP/activin A chimera is superior to native BMPs and induces bone repair in nonhuman primates when delivered in a composite matrix

Howard Seeherman, Stephen P. Berasi, Christopher Brown et al. · Science Translational Medicine · 2019 · 66 citations

Gene Therapy Corrects Brain and Behavioral Pathologies in CLN6-Batten Disease

Jacob T. Cain, Shibi Likhite, Katherine A. White et al. · Molecular Therapy · 2019 · 53 citations · Full text

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