Shibi Likhite

Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy

Jerry R. Mendell, Samiah Al-Zaidy, Richard Shell et al. · New England Journal of Medicine · 2017 · 2.2K citations · Full text

Direct conversion of patient fibroblasts demonstrates non-cell autonomous toxicity of astrocytes to motor neurons in familial and sporadic ALS

Kathrin Meyer, Laura Ferraiuolo, Carlos J. Miranda et al. · Proceedings of the National Academy of Sciences · 2013 · 347 citations · Full text

Improving Single Injection CSF Delivery of AAV9-mediated Gene Therapy for SMA: A Dose–response Study in Mice and Nonhuman Primates

Kathrin Meyer, Laura Ferraiuolo, Leah Schmelzer et al. · Molecular Therapy · 2014 · 269 citations · Full text

Oligodendrocytes contribute to motor neuron death in ALS via SOD1-dependent mechanism

Laura Ferraiuolo, Kathrin Meyer, Thomas W. Sherwood et al. · Proceedings of the National Academy of Sciences · 2016 · 180 citations · Full text

Major histocompatibility complex class I molecules protect motor neurons from astrocyte-induced toxicity in amyotrophic lateral sclerosis

SungWon Song, Carlos J. Miranda, Lyndsey Braun et al. · Nature Medicine · 2016 · 140 citations · Full text

Amyotrophic Lateral Sclerosis, Medicine, Protect Motor Neurons +9