Carlos J. Miranda

Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy

Jerry R. Mendell, Samiah Al-Zaidy, Richard Shell et al. · New England Journal of Medicine · 2017 · 2.3K citations · Full text

Medicine, Genetics, Neurology +16

Microglia Induce Motor Neuron Death via the Classical NF-κB Pathway in Amyotrophic Lateral Sclerosis

Laura Ferraiuolo, Amanda Haidet-Phillips, Leah Schmelzer et al. · Neuron · 2014 · 636 citations

Life Sciences, Neurobiology, Neuroscience +16

Direct conversion of patient fibroblasts demonstrates non-cell autonomous toxicity of astrocytes to motor neurons in familial and sporadic ALS

Kathrin Meyer, Laura Ferraiuolo, Carlos J. Miranda et al. · Proceedings of the National Academy of Sciences · 2013 · 352 citations · Full text

Life Sciences, Neurobiology, Neuroscience +17

Rapid and Efficient Generation of Functional Motor Neurons From Human Pluripotent Stem Cells Using Gene Delivered Transcription Factor Codes

Mark E. Hester, Matthew Murtha, SungWon Song et al. · Molecular Therapy · 2011 · 183 citations · Full text

Life Sciences, Developmental Biology, Neuroscience +17

Oligodendrocytes contribute to motor neuron death in ALS via SOD1-dependent mechanism

Laura Ferraiuolo, Kathrin Meyer, Thomas W. Sherwood et al. · Proceedings of the National Academy of Sciences · 2016 · 181 citations · Full text

Life Sciences, Neurobiology, Neuroscience +17