Anchel González‐Barriga

The expanded CAG repeat in the huntingtin gene as target for therapeutic RNA modulation throughout the HD mouse brain

Nicole A. Datson, Anchel González‐Barriga, Eleni Kourkouta et al. · PLoS ONE · 2017 · 71 citations · Full text

Life Sciences, Neurology, Neuroscience +17

Suppression of Mutant Protein Expression in SCA3 and SCA1 Mice Using a CAG Repeat-Targeting Antisense Oligonucleotide

Eleni Kourkouta, Rudie Weij, Anchel González‐Barriga et al. · Molecular Therapy — Nucleic Acids · 2019 · 61 citations · Full text

Life Sciences, Genetics, Neurology +17

A low absolute number of expanded transcripts is involved in myotonic dystrophy type 1 manifestation in muscle

Anke E. E. G. Gudde, Anchel González‐Barriga, Walther J. A. A. van den Broek et al. · Human Molecular Genetics · 2016 · 45 citations · Full text

Life Sciences, Genetics, Molecular Biology +16

Design and Analysis of Effects of Triplet Repeat Oligonucleotides in Cell Models for Myotonic Dystrophy

Anchel González‐Barriga, Susan Mulders, Jeroen van de Giessen et al. · Molecular Therapy — Nucleic Acids · 2013 · 43 citations · Full text

Life Sciences, Genetics, Molecular Biology +14

Intracellular Distribution and Nuclear Activity of Antisense Oligonucleotides After Unassisted Uptake in Myoblasts and Differentiated Myotubes <i>In Vitro</i>

Anchel González‐Barriga, Bram Nillessen, Julia Kranzen et al. · Nucleic Acid Therapeutics · 2017 · 30 citations · Full text

Life Sciences, Cell Biology, Molecular Biology +16