Ron Baik

High-Efficiency, Selection-free Gene Repair in Airway Stem Cells from Cystic Fibrosis Patients Rescues CFTR Function in Differentiated Epithelia

Sriram Vaidyanathan, Ameen A. Salahudeen, Zachary M. Sellers et al. · Cell stem cell · 2019 · 132 citations · Full text

Life Sciences, Cell Biology, Molecular Biology +15

Cas9-AAV6 gene correction of beta-globin in autologous HSCs improves sickle cell disease erythropoiesis in mice

Adam C. Wilkinson, Daniel P. Dever, Ron Baik et al. · Nature Communications · 2021 · 100 citations · Full text

Medicine, Biotechnology, Hematology +16

Targeted replacement of full-length CFTR in human airway stem cells by CRISPR-Cas9 for pan-mutation correction in the endogenous locus

Sriram Vaidyanathan, Ron Baik, Lü Chen et al. · Molecular Therapy · 2021 · 69 citations · Full text

Life Sciences, Biotechnology, Genetics +17

Transient inhibition of 53BP1 increases the frequency of targeted integration in human hematopoietic stem and progenitor cells

Ron Baik, M. Kyle Cromer, Steve E. Glenn et al. · Nature Communications · 2024 · 27 citations · Full text

Life Sciences, Genetics, Molecular Biology +17

Cas9-AAV6 Gene Correction of Beta-Globin in Autologous HSCs Improves Sickle Cell Disease Erythropoiesis in Mice

Adam C. Wilkinson, Daniel P. Dever, Ron Baik et al. · bioRxiv (Cold Spring Harbor Laboratory) · 2020 · 12 citations · Full text

Medicine, Biotechnology, Hematology +16