Francesca Ciotti

Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access

Francesca Fumagalli, Valeria Calbi, Maria Grazia Natali Sora et al. · The Lancet · 2022 · 266 citations · Full text

Intra‐arterial transplantation of <scp>HLA</scp> ‐matched donor mesoangioblasts in Duchenne muscular dystrophy

Giulio Cossu, Stefano C. Previtali, Sara Napolitano et al. · EMBO Molecular Medicine · 2015 · 165 citations · Full text

Health related quality of life in Middle Eastern children with beta-thalassemia

Giovanni Caocci, Fabio Efficace, Francesca Ciotti et al. · BMC Blood Disorders · 2012 · 109 citations · Full text

Metachromatic leukodystrophy: A single‐center longitudinal study of 45 patients

Francesca Fumagalli, Alberto A. Zambon, Paola M. V. Rancoita et al. · Journal of Inherited Metabolic Disease · 2021 · 71 citations · Full text

Prospective Assessment of Health-Related Quality of Life in Pediatric Patients with Beta-Thalassemia following Hematopoietic Stem Cell Transplantation

Giovanni Caocci, Fabio Efficace, Francesca Ciotti et al. · Biology of Blood and Marrow Transplantation · 2010 · 61 citations · Full text

Quality Of Life, Health-related Quality, Translational Medicine +16