Paola M. V. Rancoita

Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial

Maria Sessa, Laura Lorioli, Francesca Fumagalli et al. · The Lancet · 2016 · 496 citations

Ad-hoc Analysis, Cell Therapy, Bone Marrow Failure +8

The 2021 WHO catalogue of Mycobacterium tuberculosis complex mutations associated with drug resistance: a genotypic analysis

Paolo Miotto, Claudio U. Köser, Philip W. Fowler et al. · The Lancet Microbe · 2022 · 282 citations · Full text

Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access

Francesca Fumagalli, Valeria Calbi, Maria Grazia Natali Sora et al. · The Lancet · 2022 · 266 citations · Full text

Two main genetic pathways lead to the transformation of chronic lymphocytic leukemia to Richter syndrome

Ekaterina Chigrinova, Andrea Rinaldi, Ivo Kwee et al. · Blood · 2013 · 248 citations · Full text

The NF-κB negative regulator TNFAIP3 (A20) is inactivated by somatic mutations and genomic deletions in marginal zone lymphomas

Urban Novak, Andrea Rinaldi, Ivo Kwee et al. · Blood · 2009 · 240 citations · Full text