Concepedia
Statistics
Publications
85
Citations
4.4K
H-Index
36
Active since
2001
Affiliations
UNSW Sydney(Current)
Sydney Children's Hospital
The University of Sydney
Sydney Children’s Hospitals Network
Children's Hospital at Westmead
Michelle A. Farrar is an author at UNSW Sydney specializing in medicine, pediatrics, and neurology.
Publications per year
2001–2025
Onasemnogene abeparvovec for presymptomatic infants with two copies of SMN2 at risk for spinal muscular atrophy type 1: the Phase III SPR1NT trial
Kevin A. Strauss, Michelle A. Farrar, Francesco Muntoni et al. · Nature Medicine · 2022 · 295 citations · Full text
Medicine, Genetics, Pediatrics +13
Onasemnogene abeparvovec for presymptomatic infants with three copies of SMN2 at risk for spinal muscular atrophy: the Phase III SPR1NT trial
Kevin A. Strauss, Michelle A. Farrar, Francesco Muntoni et al. · Nature Medicine · 2022 · 276 citations · Full text
Medicine, Genetics, Pediatrics +16
Thrombotic Microangiopathy Following Onasemnogene Abeparvovec for Spinal Muscular Atrophy: A Case Series
Deepa H. Chand, Craig M. Zaidman, Kapil Arya et al. · The Journal of Pediatrics · 2020 · 201 citations · Full text
Medicine, Neurology, Pediatrics +13
Newborn screening programs for spinal muscular atrophy worldwide: Where we stand and where to go
Tamara Dangouloff, Eva Vrščaj, Laurent Servais et al. · Neuromuscular Disorders · 2021 · 172 citations
Medicine, Pediatrics, Preventive Medicine +12
The implementation of newborn screening for spinal muscular atrophy: the Australian experience
Didu Kariyawasam, Jacqueline S. Russell, Veronica Wiley et al. · Genetics in Medicine · 2019 · 168 citations · Full text
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