Heather Lau

Evaluating the massive underreporting and undertesting of COVID-19 cases in multiple global epicenters

Heather Lau, Tanja Khosrawipour, Piotr Kocbach et al. · Pulmonology · 2020 · 350 citations · Full text

Safety and efficacy of cipaglucosidase alfa plus miglustat versus alglucosidase alfa plus placebo in late-onset Pompe disease (PROPEL): an international, randomised, double-blind, parallel-group, phase 3 trial

Benedikt Schoser, Mark Roberts, Barry J. Byrne et al. · The Lancet Neurology · 2021 · 124 citations

Clinical Trials, Cipaglucosidase Alfa, Pharmacotherapy +2

Demographics and patient characteristics of 1209 patients with Gaucher disease: Descriptive analysis from the Gaucher Outcome Survey (GOS)

Ari Zimran, Nadia Belmatoug, Bruno Bembi et al. · American Journal of Hematology · 2017 · 92 citations · Full text

Gaucher Outcome Survey, Family Medicine, Population Children +15

A phase 3 randomized study evaluating sialic acid extended-release for GNE myopathy

Hanns Lochmüller, Anthony Béhin, Yoseph Caraco et al. · Neurology · 2019 · 77 citations · Full text

Prophylaxis of Radiation-Associated Mucositis in Conventionally Treated Patients With Head and Neck Cancer: A Double-Blind, Phase III, Randomized, Controlled Trial Evaluating the Clinical Efficacy of an Antimicrobial Lozenge Using a Validated Mucositis Scoring System

S. El-Sayed, Abdenour Nabid, Wendy Shelley et al. · Journal of Clinical Oncology · 2002 · 75 citations